The recent deliberations by the FDA’s Cardiovascular and Renal Drugs Advisory Committee regarding elamipretide as a treatment for Barth syndrome have cast a spotlight on the challenges of drug approval for ultra-rare diseases. Barth syndrome, a disorder primarily affecting boys, results from mutations in the TAFAZZIN gene and is characterized by severe complications such as
Health
As Hurricane Milton approaches the southeastern coast, federal officials and medical manufacturers are on high alert. The impending storm poses a significant threat to the already tenuous supply chain of critical hospital supplies, particularly intravenous (IV) fluids. This situation is exacerbated by the recent flooding at a major manufacturing facility in North Carolina, which damaged
Substantial concerns about the proliferation of unverified stem cell therapies have prompted calls for tighter regulations. Recent findings from research conducted in Australia and Canada offer compelling evidence that regulatory frameworks can significantly reduce the number of companies marketing these dubious treatments. By assessing the impact of recent policy changes, experts have indicated that effective
In a historic announcement on Tuesday, the Biden administration unveiled a comprehensive mandate that orders every water system across the United States to eradicate legacy lead pipes within a decade. This significant step comes in response to overwhelming evidence indicating the dangers posed by lead in drinking water—a threat that has persisted for far too
The residency application process is undergoing a significant transformation. Preliminary data from the Association of American Medical Colleges (AAMC) reveals that in 2025, applicants are submitting fewer applications compared to previous years while concurrently reducing their financial burden. This change follows AAMC’s overhaul of its pricing structure for the Electronic Residency Application Service (ERAS) intended
Pediatric obesity is rapidly becoming a significant public health concern, with long-term implications for both physical and mental health. As rates among children and adolescents continue to rise, healthcare professionals are increasingly tasked with determining appropriate intervention strategies. In particular, for specialists in pediatric obesity medicine, like myself, the focus is shifting toward not only
In recent years, conversations surrounding women’s health have begun to gain momentum, yet there remains a critical gap in the approach to pain management during gynecological procedures. Patients often find themselves caught off guard by the discomfort they experience, leading to audible expressions of distress that highlight a broader issue within the healthcare system. The
In a recent investigation led by Dr. Stefan Brunner and his team at the LMU Klinikum University Hospital in Munich, Germany, researchers sought to elucidate the relationship between binge drinking behavior and its implications on heart health, particularly focusing on the occurrence of arrhythmias. The study, known as MunichBREW II, aimed to shed light on
Artificial Intelligence (AI) has permeated various fields, including healthcare, where it’s starting to transform the landscape of medical diagnostics. One intriguing area is the use of deep learning algorithms in analyzing MRI scans, specifically for conditions such as axial spondyloarthritis (axSpA). Researchers have made strides in developing AI systems that aim to match or surpass
The complexities surrounding healthcare in the United States have long been a source of both concern and intrigue, especially in light of current investigative reports. From the grim realities of abortion care to alarming safety deficiencies in food processing, recent editions of investigative journalism shed light on the troubling state of affairs in the field.